Amylyx Pharmaceuticals Inc.

Amylyx Pharmaceuticals Inc. Ushering in a new era for treating diseases with high unmet needs

06/08/2026

Amylyx is presenting two posters at the Endocrine Society’s Annual Meeting, . We look forward to sharing insights on the burden of PBH in the U.S. on healthcare resource utilization, economic impact, and quality of life, as well as participant-centric trial design considerations for our pivotal Phase 3 LUCIDITY clinical trial.

See presentation details below and in today’s release: https://bit.ly/43q7AKv

Next week, Amylyx’s Chief Medical Officer Bedrosian, MD, will be a panelist at the World Orphan Drug Congress USA 2026 ...
06/05/2026

Next week, Amylyx’s Chief Medical Officer Bedrosian, MD, will be a panelist at the World Orphan Drug Congress USA 2026 taking place here in Boston. See session details below!

is heading to the American Diabetes Association’s 2026 Scientific Sessions in New Orleans. We hope to see you there!
06/03/2026

is heading to the American Diabetes Association’s 2026 Scientific Sessions in New Orleans. We hope to see you there!

This week, is at the Wolfram Syndrome UK’s International Researcher’s Symposium, where we’re presenting updates on our...
06/02/2026

This week, is at the Wolfram Syndrome UK’s International Researcher’s Symposium, where we’re presenting updates on our Phase 2 HELIOS trial in Wolfram syndrome. More details below.

In recognition of Mental Health Awareness Month, we took time to step away from Anchor Week updates and recharge with ha...
05/29/2026

In recognition of Mental Health Awareness Month, we took time to step away from Anchor Week updates and recharge with hands-on, creative activities. These are the moments that help strengthen our community and support a culture of care.

05/22/2026

Wolfram syndrome is a rare genetic disorder that affects approximately 3,000 people living in the U.S. with no approved treatment options.

Common manifestations of Wolfram syndrome include insulin-requiring diabetes mellitus, vision loss, diabetes insipidus, hearing loss, neurogenic bladder, impaired balance and coordination, and difficulty breathing that can progress to respiratory failure. Learn more about Wolfram syndrome on our website at https://www.amylyx.com/

05/15/2026

We’re pleased to share that Week 24 and Week 48 results from our Phase 2 open-label HELIOS clinical trial in Wolfram syndrome have been published in the Journal of Clinical Investigation. These findings indicate continued improvement in pancreatic function and visual acuity stabilization over 48 weeks, as well as a generally well-tolerated safety profile. Read more in today’s release: https://www.amylyx.com/news/amylyx-pharmaceuticals-announces-peer-reviewed-publication-of-phase-2-open-label-helios-trial-data-for-amx0035-in-the-journal-of-clinical-investigation

05/12/2026

Calpain-2 (CAPN2) is an important contributor to axonal degeneration, or nerve fiber damage, which plays a critical role in ALS progression.

Research suggests that when calpain-2 becomes overactive, it can interfere with normal cell function and weaken the nerve fibers that carry signals throughout the body.

Learn more about the connection between calpain-2 and ALS on our website at https://bit.ly/4u9G3J5

05/05/2026

We’re pleased to announce the launch of a U.S. expanded access program (EAP) for post-bariatric hypoglycemia (PBH). See today’s press release for more information: https://bit.ly/42LEzZh

Additional information about the EAP is available at amylyx.com/global-access-policy.

04/29/2026

Post-bariatric hypoglycemia (PBH) is a rare, chronic condition with no FDA-approved treatments. Among the roughly two million people who have had Roux-en-Y gastric bypass (RYGB) or sleeve gastrectomy in the past decade in the U.S., an estimated 160,000 are living with PBH today.

The condition can cause debilitating low blood sugar episodes when the brain does not receive enough glucose. PBH can be difficult to diagnose as symptoms, such as brain fog, fatigue, sweating, blurred vision, and dizziness, can be non-specific, vary in severity, and/or be mistaken for dumping syndrome. Learn more about PBH on our website at https://bit.ly/4cCeodq

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