Cure GM1 Foundation

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Cure GM1 Foundation

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The Cure GM1 Foundation is dedicated to directly funding research for a cure for GM1 Gangliosidosis.

Awareness -> Funding -> Hope
Donate to Save Children: https://www.curegm1.org/donate
The only 501(c)(3) entirely dedicated to GM1, Founded by families impacted by GM1 gangliosidosis, a fatal disease that primarily impacts children.

10/28/2026

🎃 Show Us Your Halloween Spirit! 👻
We love seeing our incredible GM1 community celebrate Halloween in creative and fun ways. Whether it's spooky, silly, sweet, or superhero themed, we want to see your costumes!
Share your favorite costume photo with us for a chance to be featured on Cure GM1 Foundation's social media and help spread smiles throughout our community.
Submit your photo here:
https://www.curegm1.org/share-a-quote/
Thank you for sharing your Halloween memories with us. We can't wait to see everyone's amazing costumes! 🧡

10/27/2026

Halloween should be welcoming for every child! 🎃

This season, let's create a world where every trick-or-treater feels celebrated. A little flexibility can make the celebration more accessible. Be patient. Offer different ways to participate. Welcome every costume, communication style, and pace. Wishing everyone in the GM1 community and beyond a joyful, inclusive Halloween!

10/26/2026

Research Is Brewing! 🍂 Why do natural history studies matter in GM1 gangliosidosis?

These vital studies help researchers understand how GM1 changes over time, tracking family milestones, medical charts, and other crucial information. Every piece of information can strengthen future research!

Learn more about the importance of natural history studies: curegm1.org/matrix

10/25/2026

Halloween is a fun night for many families, but for children living with GM1 and other disabilities, it can also bring unique challenges.
As you welcome trick or treaters this year, remember that not every child can say "trick or treat," carry their own candy bucket, or walk to your door independently. Some may communicate differently, use mobility devices, or need a little extra patience and understanding.
A smile, kindness, and a little flexibility can make Halloween a magical experience for every child.
Let's help make Halloween inclusive for everyone. 🧡

10/24/2026

Halloween is a special time, and we believe every child deserves to celebrate the magic of the season. For families in our GM1 community and all families with disabled children, a thoughtful approach can ensure a wonderful and inclusive experience.

Consider accessible trick or treating routes, comfortable costumes that allow for mobility, and sensory friendly options like quiet times or noise reducing headphones. Communication supports like visual cards can help too. For food allergies and medical needs, participating in the Teal Pumpkin Project or having non food treats ready can make a difference. Remember, flexible celebrations from home parties to trunk or treat events offer joy for everyone.

We encourage neighbors to be patient, welcoming, and understand that every child participates differently. Let's work together to make Halloween accessible and filled with hope for every child.

Join us in making Halloween welcoming and joyful for all.

10/23/2026

Keeping track of a child's care with GM1 means managing mountains of paperwork. Through our partnership with Basion, GM1 families now have access to a free companion tool to help carry the load.
Key features for GM1 families:
• Organizes medical records into a single timeline
• Answers medical questions with clear, cited sources
• Prepares summaries before specialist appointments
• Tracks nearby clinical trials and support groups
• 100% HIPAA compliant
Basion is free for GM1 families through Cure GM1.
Sign up at basion.ai/organization/cure-gm1-foundation

10/23/2026

On October 2, families, clinicians and researchers from around the world gathered for the 2026 International GM1 Virtual Community Conference. 💚

Our recap covers family stories, research updates, practical caregiver advice and ways to help.

“We are rare, and today we are not alone.”

Read the full recap: curegm1.org/gm1-conference-2026-highlights

10/22/2026

Every gene therapy for GM1 gangliosidosis is working toward the same goal: giving cells a healthy copy of the GLB1 gene so they can make the enzyme beta-galactosidase. Researchers are taking two main roads to get there.

AAV gene therapy uses a harmless virus to carry a working GLB1 gene into a patient's own cells, usually in a single infusion. It is the approach furthest along in human GM1 trials, and the first 3-year NIH results were published in 2026.

Ex vivo lentiviral gene therapy corrects a patient's own blood stem cells in the lab and gives them back, creating a lifelong supply of enzyme. For GM1 it is still at the research stage, and a 2025 mouse study showed improved motor function and longer survival.

Swipe through to compare them, then read the full guide, medically reviewed by Simon A. Jones, MBChB, BSc, MRCPCH and Aimee Donald, MBChB, PhD: https://www.curegm1.org/aav-vs-lentiviral-gene-therapy-gm1/

Having more than one serious approach in development is one of the most hopeful signs in GM1 research today.

For education and support. Not medical advice.

10/21/2026

GM1 is rare, and every story shared builds awareness and brings us closer to a cure. Thank you to the families who so bravely shared their journeys. Your courage gives hope to others.

You can now browse stories by GM1 type at curegm1.org/stories 💚

Address

PO Box 6890
Albany, CA
94706

Telephone

+15103062460

Website

http://www.curegm1.org/

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