Rare Disease Research

10/13/2026

RDR is coming to Orlando this weekend for the Global Site Solutions Summit 😎🌴

Come visit us at Booth 1115 and connect with our team, find out what we're currently working on and how we can collaborate in the future.

10/08/2026

📣📣📣Attention community 📣📣📣

RDR is looking for participants for a PKU trial at our North Carolina and Florida locations 😎

For more information, visit our website and the Otsuka website below:
https://trials.otsuka-us.com/trials/JNT517-301

09/09/2026

Navigating treatment options can bring up a lot of questions.

If you're exploring whether a clinical trial at Rare Disease Research might be an option for you, there's now an easy way to find out.

RDR and myTomorrows are working together to open up access to clinical trials.

Together, we can help you learn about opportunities at RDR and connect with the team.

You can now book a free call with a myTomorrows patient navigator, a trained professional with a medical background who can help you:

✅ Understand which clinical trials are currently recruiting at RDR
✅ Review whether you may meet the initial eligibility criteria
✅ Explore what your next steps could look like

The call is free and there's no obligation – asking for information doesn't commit you to joining a trial.

Navigators are there to help you understand your options and answer any questions you have. They don't give medical advice or replace your own care team, and any final eligibility is confirmed by the RDR team.

Whenever you're ready, the team is here to help.

�� Book a free call: https://mytomorro.ws/0w1

�� Learn more: https://mytomorro.ws/7439bb

Rare Disease Research (RDR) is fully dedicated to clinical studies for rare conditions.

09/04/2026

Access changes lives !

Since 2024, the United Nations has recognized September 7th as World Duchenne Awareness Day 💖

Get informed, get involved.

https://www.parentprojectmd.org/get-involved/wdad/

08/14/2026

🎊🎆 August is Spinal Muscular Atrophy Awareness Month🎆🎊

Visit our friends at CureSMA.org for more information about SMA, events near you and other ways to help this community that is so dear to our hearts💜

August is SMA Awareness month, and we are so excited to be celebrating with all of you!

Every research grant funded, every clinical trial advanced, every family supported, none of it happens alone. It takes our incredible community continuing to show up.

This month, we're celebrating researchers pushing science forward, families living with SMA and the supporters who make our work possible.

Follow along all August for stories, spotlights and other ways to get involved 💜🧡

08/11/2026

We are honored to be named this year's Rare Disease Clinical Trial Company of the Year by Life Sciences Review Magazine!

Read more about the interview with our CEO and Founder Han Phan below:

https://www.lifesciencesreview.com/digital/August2026/Gene_Therapy_and_Revolutionary_Cancer/

08/05/2026

Edward Smith, MD, a neurologist, explains why he avoids judgmental approaches to noncompliance and instead focuses on trust, understanding barriers to care, and collaborative decision-making with patients and families.

Edward Smith, MD, explains how open, judgment-free conversations about Duchenne noncompliance can support shared decision-making.

06/18/2026

Rare Disease Research, LLC will be at the PPMD Conference next week!

🌴 Stop by booth #25 and connect with our team 🌴

06/04/2026

June is Dravet Syndrome awareness month!

05/20/2026

On this Clinical Trials Day, we celebrate our study participants, their families, coordinators, physicians, researchers, advocates, and the countless hands working tirelessly in the background to advance science and improve lives. Thank you for shaping the future of medicine and rising above the challenges that come with venturing into the unknown!